Peer-to-Peer Campaign
Peer-to-Peer Campaign: AAV Project and Other Research

Money Raised: $115,743.55  Campaign Goal: $250,000.00

 

With funds raised from the AHC Foundation, we will support AAV gene therapy and other research related to the project.  We believe a path has been identified to a viable permanent treatment: gene therapy.  The gene therapy we propose will involve inserting a functional copy of the ATP1A3 gene into a virus (an adeno-associated virus or AAV) that has been stripped of its harmful payload and its ability to reproduce. The virus will then be injected into the cerebrospinal fluid and will carry the functional gene to the cells in the brain that are failing. By delivering additional functional copies of the gene, we should be able to rescue those cells, and treat the disease permanently. 

Learn more about the project here. 

 

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Stacie Matuska
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  Raised: $82,719.78
  Goal: $100,000.00

 
For Landry
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  Raised: $10,074.77
  Goal: $50,000.00

 
Heather Gates

  Raised: $3,350.00
  Goal: N/A

 
Laura's Mission to Cure AHC
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  Raised: $2,690.00
  Goal: $1,000.00

 
Paul Hodes
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  Raised: $1,335.00
  Goal: $5,000.00

 
Elisaveta Katsarova
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  Raised: $1,291.00
  Goal: $2,000.00

 
Stormy's Help Find a Cure for AHC Fundraising Page
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  Raised: $1,050.00
  Goal: $250,000.00

 
Keira's Fundraising Page
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  Raised: $550.00
  Goal: $2,000.00

 
Dax Heimgartner's Fundraising Page
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  Raised: $500.00
  Goal: $10,000.00

 
Blake Fechlie
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  Raised: $460.00
  Goal: $1,500.00

 
Sean Gerber Fundraising Page
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  Raised: $425.00
  Goal: $25,000.00

 
Coralynn Long's Fundraising Page
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  Raised: $300.00
  Goal: $5,000.00

 
Brooke Tasi
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  Raised: $275.00
  Goal: $5,000.00

 
END AHC WITH AAV (Gene Therapy Project)
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  Raised: $261.00
  Goal: $500.00

 
Alaina’s Allies to End AHC
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  Raised: $80.00
  Goal: $3,000.00

 
Kiley's Krew
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  Raised: $50.00
  Goal: $5,000.00

 
Laura Marszalek
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  Raised: $45.00
  Goal: $5,000.00

 
Karen Royce
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  Raised: $30.00
  Goal: $5,000.00

 
Lynn Egan
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  Raised: $25.00
  Goal: $5,000.00

 
Karen Newman

  Raised: $25.00
  Goal: N/A

 
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