This is our little hero Blake. He has been to hell and back 10 times over in his short life due to having AHC. We are hoping that one day there will be a cure for Blake and all the other children who suffer from this awful medical condition . Any donation will help us get closer to finding a cure for our little man and all the AHC heroes around the world.
Thank you so much xx
With funds raised from the AHC Foundation, we will support AAV gene therapy and other research related to the project. We believe a path has been identified to a viable permanent treatment: gene therapy. The gene therapy we propose will involve inserting a functional copy of the ATP1A3 gene into a virus (an adeno-associated virus or AAV) that has been stripped of its harmful payload and its ability to reproduce. The virus will then be injected into the cerebrospinal fluid and will carry the functional gene to the cells in the brain that are failing. By delivering additional functional copies of the gene, we should be able to rescue those cells, and treat the disease permanently.
|Ethan Tee||03/22/2019||$100.00||Truly hoping that my donation makes a difference.||Mercedes Smith||03/06/2019||$160.00||Love always, Auntie Cedes xxxx||Chris Sloan||03/05/2019||$100.00||Susie Allen-Fechlie||03/03/2019||$50.00||Shaun Williamson||03/01/2019||$50.00||Fingers crossed they find a cure soon! Shaun and Bern xx|