Our precious miracle, Coralynn, is 2 years old. She has been diagnosed with AHC along with Fox P1. They are both very rare disorders, especially together. God has carried our baby girl through so much, and we know He has big plans for her! We are making this page to help raise funds and awareness for AHC. We hope to help find a cure for this devastating disease. Thanks so much for your help! Please share to help raise others' awareness.
With funds raised from the AHC Foundation, we will support AAV gene therapy and other research related to the project. We believe a path has been identified to a viable permanent treatment: gene therapy. The gene therapy we propose will involve inserting a functional copy of the ATP1A3 gene into a virus (an adeno-associated virus or AAV) that has been stripped of its harmful payload and its ability to reproduce. The virus will then be injected into the cerebrospinal fluid and will carry the functional gene to the cells in the brain that are failing. By delivering additional functional copies of the gene, we should be able to rescue those cells, and treat the disease permanently.
|Coralynn Long||02/19/2019||$100.00||Love and prayers! Troy, Brenda, MaKayla, and Chloe||JoAnn & Jim Larson||02/15/2019||$100.00||Love you guys and praying for little Coralynn.||Heather Varney||02/13/2019||$100.00||Lots of love Coralyn|