With funds raised from the AHC Foundation, we will support AAV gene therapy and other research related to the project. We believe a path has been identified to a viable permanent treatment: gene therapy. The gene therapy we propose will involve inserting a functional copy of the ATP1A3 gene into a virus (an adeno-associated virus or AAV) that has been stripped of its harmful payload and its ability to reproduce. The virus will then be injected into the cerebrospinal fluid and will carry the functional gene to the cells in the brain that are failing. By delivering additional functional copies of the gene, we should be able to rescue those cells, and treat the disease permanently.
|Viv Machar||05/08/2019||$20.00||Best wishes Laura from your Cabrini friend. xo||Kate Johnstone||04/29/2019||$10.00||Good luck x||Mark Sakareassen||04/29/2019||$100.00||Love from dizzy Odin Idelle Kelda.||Earl Sakareassen||04/28/2019||$1,000.00||Love to my daughter Laura and best wishes to all AHC families.||Patterson Family||04/23/2019||$20.00||Great job Laura||Adam Snooks||04/23/2019||$50.00||Laura Sakareassen||04/21/2019||$200.00||Love & best wishes Laura, from Gran & Pop.||Cherie Ambry||04/20/2019||$50.00||All the best Laura x||Wendi Emmerson||04/20/2019||$10.00||Happy Easter xx||Gerard & Janine Op De Coul||04/20/2019||$50.00||Best wishes Laura||Elizabeth Grantham||04/20/2019||$20.00||Doing a wonderful job Laura in raising awareness||Jean Turnbull||04/20/2019||$100.00||Brilliant work!||Adam Sakareassen||04/19/2019||$100.00||Glenda Davies-Sakareassen||04/19/2019||$50.00||Angela Ewan||04/19/2019||$30.00||I wish you all the best Laura in your Quest and to make everyone aware.||Leanne N Gonzy Diez||04/19/2019||$50.00||What a superstar you are Laura!! We hope you raise heaps of money!!||TONY DOSLOV||04/19/2019||$70.00||John and Belinda Formosa||04/19/2019||$50.00||Love you Sis. Xxx||Tammie Edie||04/19/2019||$10.00||Denise Roelsnds||04/19/2019||$50.00||Your doing a wonderful job Laura, keep up the good work.||Sumi Sivalingam||04/19/2019||$100.00||What a great cause Laura, all the best in your campaign.||Jenni Davies||04/19/2019||$50.00||Well done Laura!||Vera Shepherd||04/19/2019||$200.00||Yvonne Davies||04/19/2019||$100.00||Ingrid Czerniecki||04/19/2019||$50.00||For you Laura,love Aunty Ingrid xx||Angela Cheng||04/19/2019||$50.00|